Please read and agree to the
terms and conditions
of this site.
I agree
Stream
/tech
Clear filters and search
Format
photo
Tags
biotech
life sciences
national blog main
rare diseases
7
×
boston
boston blog main
boston top stories
fda
clinical trials
rare disease drugs
alexion pharmaceuticals
alpha-1 antitrypsin
cystic fibrosis
deals
eculizumab
geoffrey porges
paroxysmal nocturnal hemoglobinuria
ravulizumab
svb leerink
vertex pharmaceuticals
achillion pharmaceuticals
acute hepatic porphyria
alnylam pharmaceuticals
alström syndrome
amgen
arch venture partners
arrowhead pharmaceuticals
atypical hemolytic uremic syndrome
avotrombopag
bardet-biedl syndrome
beta-thalassemia
biosimilars
blood platelets
cancer
chemotherapy
chronic liver disease
complement system
crispr therapeutics
danicopan
douglas melton
What
pharmaceuticals
7
×
drug
disease
rare
alexion
approval
biotech
developed
fda
million
phase
vertex
won
achillion
acquire
acquiring
acquisition
agrees
alnylam
amgen
bets
biosimilar
buy
cell
challenge
company
completed
deal
deficiency
developing
diabetes
dimming
disorder
disorders
dova
exclusivity
experimental
extend
filing
firms
Language
unset
7
×
Current search:
pharmaceuticals
×
" rare diseases "
×
unset
×
{{ ::tile.facetWhoCard }}
{{ ::tile.pubDate | moment: 'fromNow'}}
Paste
[[item:{{::tile.id}}]]
to render this photo inside an other item's description.
PROCESSING
TRANSCODING
ERROR
EXTRACTING
ERROR
{{::tile.title}}